Immune responses Gene Transfer Capsid Click chemistry Beta-subunit Assembly-activating protein GRMD dog Calcium Humoral immunity AAP Adeno-associated virus Clinical trial AAV vectors Skeletal muscle Baculovirus Dose study Vector Centronuclear myopathy Inherited retinal dystrophies Cell therapy Bioorthogonality Duchenne muscular dystrophy AAV vector Gene Therapy Eye surgery Genes Adenoviridae/immunology Exon skipping Age Cerebellum Infectivity Intrathymic gene transfer Duchenne Childhood blindness Ectopic expression Cell–virus interaction Gait assessment Immunogenicity inflammation gene therapy AAV Immune response High-throughput technology Identity CMC GC-content Treg Bioconjugates GRMD DMDmdx rat Adenoassociated viral vector Baculovirus expression vector Engineering Impurities Immunomodulation Fluid-air exchange Animal model Congenital amaurosis Gene-therapy Accelerometry Clinical trials Manufacturing Animals Homologous recombination Dystrophin ABCA4 Intra-cerebrospinal fluid injection Human-monocyte-derived dendritic cells Intravitreal Homopolymers Crigler–Najjar Syndrome Air tamponade Homogeneity B-Lymphocytes/immunology/metabolism Acute treatment Antibodies/immunology/metabolism Cone photoreceptors Gene therapy DMD In vivo AAV Analytical ultracentrifugation Gene transfer Capsid assembly Mice Capsid thermostability Immunogenicity Insect cells Quality control Antibody responses CNS AUC Immunosuppression CD8 + T lymphocytes Tolerance Identity assay Exercise Capsid thermal stability High-throughput sequencing Discriminant analysis Inflammation Innate immunity Dynamin 2